Obchod Ionis Pharmaceuticals, Inc. - IONS CFD
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Rozpätie | 0.22 | ||||||||
Nočný poplatok dlhej pozície
Long position overnight fee
Prejsť na platformu | -0.025457% | ||||||||
Nočný poplatok krátkej pozície
Short position overnight fee
Prejsť na platformu | 0.003235% | ||||||||
Nočný poplatok | 21:00 (UTC) | ||||||||
Minimálne množstvo na obchodovanie | 1 | ||||||||
Mena | USD | ||||||||
Marža | 20% | ||||||||
Burza cenných papierov | United States of America | ||||||||
Provízia pri predaji | 0% |
*Information provided by Capital.com
Ionis Pharmaceuticals Inc ESG Risk Ratings
‘B’ score indicates good relative ESG performance and above average degree of transparency in reporting material ESG data publicly.
Predchádzajúce Zavrieť* | 40.52 |
Otvoriť* | 40.91 |
1-ročná zmena* | 17.02% |
Denný rozsah* | 40.12 - 41.82 |
Rozsah 52 týždňov | 32.69-48.82 |
Priemerný objem (10 dní) | 1.65M |
Priemerný objem (3 mesiace) | 23.10M |
Trhová kapitalizácia | 5.80B |
Pomer P/E | -100.00K |
Zdieľa mimoriadne | 143.09M |
Výnosy | 575.97M |
EPS | -2.31 |
Dividenda (udalosť %) | N/A |
Beta | 0.52 |
Ďalší dátum zárobku | Aug 7, 2023 |
Všetky údaje poskytuje spoločnosť Refinitiv, okrem údajov označených hviezdičkou, čo sú *údaje poskytnuté Capital.com
- Last Week
- Last Month
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- Max
- Daily
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- Monthly
Date | Zatvorenie | Change | Change (%) | Otvorenie | High | Low |
---|---|---|---|---|---|---|
Jun 8, 2023 | 41.44 | 1.01 | 2.50% | 40.43 | 41.86 | 40.03 |
Jun 7, 2023 | 40.52 | 0.03 | 0.07% | 40.49 | 41.57 | 40.00 |
Jun 6, 2023 | 43.27 | 1.49 | 3.57% | 41.78 | 43.37 | 41.48 |
Jun 5, 2023 | 42.13 | 0.89 | 2.16% | 41.24 | 42.37 | 41.03 |
Jun 2, 2023 | 41.71 | 0.52 | 1.26% | 41.19 | 43.27 | 41.08 |
Jun 1, 2023 | 42.94 | 3.49 | 8.85% | 39.45 | 43.03 | 39.45 |
May 31, 2023 | 40.73 | 0.71 | 1.77% | 40.02 | 41.21 | 39.74 |
May 30, 2023 | 40.51 | 0.26 | 0.65% | 40.25 | 41.55 | 39.84 |
May 26, 2023 | 40.60 | 2.27 | 5.92% | 38.33 | 40.83 | 38.33 |
May 25, 2023 | 39.13 | -0.39 | -0.99% | 39.52 | 41.57 | 38.89 |
May 24, 2023 | 41.24 | -0.58 | -1.39% | 41.82 | 42.47 | 41.09 |
May 23, 2023 | 42.16 | 1.62 | 4.00% | 40.54 | 43.42 | 40.54 |
May 22, 2023 | 40.61 | 1.75 | 4.50% | 38.86 | 40.81 | 37.78 |
May 19, 2023 | 39.02 | 3.61 | 10.19% | 35.41 | 39.31 | 35.41 |
May 18, 2023 | 36.58 | 2.03 | 5.88% | 34.55 | 36.70 | 34.55 |
May 17, 2023 | 36.13 | 1.42 | 4.09% | 34.71 | 36.29 | 34.70 |
May 16, 2023 | 35.79 | 0.93 | 2.67% | 34.86 | 35.96 | 34.81 |
May 15, 2023 | 36.09 | 0.68 | 1.92% | 35.41 | 36.39 | 34.70 |
May 12, 2023 | 35.38 | 0.05 | 0.14% | 35.33 | 35.68 | 35.16 |
May 11, 2023 | 35.48 | 0.79 | 2.28% | 34.69 | 35.72 | 34.69 |
Ionis Pharmaceuticals, Inc. Events
Čas (UTC) (UTC) | Krajina | Udalosť |
---|---|---|
Monday, June 12, 2023 | ||
Čas (UTC) (UTC) 16:20 | Krajina US
| Udalosť Ionis Pharmaceuticals Inc at Goldman Sachs Healthcare Conference Ionis Pharmaceuticals Inc at Goldman Sachs Healthcare ConferenceForecast -Previous - |
Monday, August 7, 2023 | ||
Čas (UTC) (UTC) 12:30 | Krajina US
| Udalosť Q2 2023 Ionis Pharmaceuticals Inc Earnings Release Q2 2023 Ionis Pharmaceuticals Inc Earnings ReleaseForecast -Previous - |
Tuesday, November 7, 2023 | ||
Čas (UTC) (UTC) 13:30 | Krajina US
| Udalosť Q3 2023 Ionis Pharmaceuticals Inc Earnings Release Q3 2023 Ionis Pharmaceuticals Inc Earnings ReleaseForecast -Previous - |
- Výročný
- Štvrťročne
2022 | 2021 | 2020 | 2019 | 2018 | |
---|---|---|---|---|---|
Celkové príjmy | 587.367 | 810.456 | 729.264 | 1122.6 | 599.674 |
Výnosy | 587.367 | 810.456 | 729.264 | 1122.6 | 599.674 |
Náklady na výnosy, celkom | 14.116 | 10.842 | 11.947 | 4.384 | 1.82 |
Hrubý zisk | 573.251 | 799.614 | 717.317 | 1118.21 | 597.854 |
Celkové prevádzkové náklady | 997.558 | 849.269 | 901.346 | 822.912 | 661.046 |
Predaj/Všeobecné/Správca. Náklady, Celkom | 150.295 | 170.947 | 332.222 | 286.644 | 244.622 |
Výskum a vývoj | 833.147 | 634.953 | 526.877 | 465.688 | 414.604 |
Nezvyčajné výdavky (príjem) | 32.527 | 30.3 | 66.196 | 0 | |
Prevádzkový príjem | -410.191 | -38.813 | -172.082 | 299.687 | -61.372 |
Úrokový príjem (výdavky), čistý neprevádzkový | 9.876 | 10.798 | 37.592 | 39.765 | -14.602 |
Iné, Net | -7.274 | -1.133 | -0.062 | -0.686 | -0.182 |
Čistý príjem pred zdanením | -257.985 | -29.148 | -134.552 | 338.766 | -76.156 |
Čistý príjem po zdanení | -269.722 | -28.597 | -479.743 | 287.259 | -117.115 |
Menšinový záujem | 0 | 0 | 35.48 | -9.116 | 58.756 |
Čistý príjem pred extra. Položky | -269.722 | -28.597 | -444.263 | 278.143 | -58.359 |
Čistý príjem | -269.722 | -28.597 | -444.263 | 278.143 | 273.741 |
Príjem k dispozícii bežnému Extra. Položky | -269.722 | -28.597 | -444.263 | 278.143 | -58.359 |
Príjem k dispozícii bežnému vr. Extra. Položky | -269.722 | -28.597 | -444.263 | 278.143 | 273.741 |
Úprava riedenia | 0 | ||||
Zriedený čistý príjem | -269.722 | -28.597 | -444.263 | 278.143 | 273.741 |
Zriedený vážený priemer akcií | 141.848 | 141.021 | 139.612 | 153.164 | 134.056 |
Zriedený EPS s výnimkou mimoriadnych položiek | -1.90149 | -0.20279 | -3.18213 | 1.81598 | -0.43533 |
Zriedený normalizovaný EPS | -2.58703 | -0.05286 | -3.04106 | 2.18246 | -0.43533 |
Celkom mimoriadne položky | 332.1 | ||||
Gain (Loss) on Sale of Assets | 149.604 |
Mar 2023 | Dec 2022 | Sep 2022 | Jun 2022 | Mar 2022 | |
---|---|---|---|---|---|
Celkové príjmy | 130.524 | 151.889 | 159.767 | 133.791 | 141.919 |
Výnosy | 130.524 | 151.889 | 159.767 | 133.791 | 141.919 |
Náklady na výnosy, celkom | 1.343 | 3.686 | 1.515 | 4.745 | 4.17 |
Hrubý zisk | 129.181 | 148.203 | 158.252 | 129.046 | 137.749 |
Celkové prevádzkové náklady | 244.672 | 359.908 | 218.921 | 219.305 | 199.423 |
Predaj/Všeobecné/Správca. Náklady, Celkom | 45.516 | 47.95 | 34.416 | 33.802 | 34.127 |
Výskum a vývoj | 197.813 | 308.272 | 182.99 | 180.758 | 161.126 |
Prevádzkový príjem | -114.148 | -208.019 | -59.154 | -85.514 | -57.504 |
Úrokový príjem (výdavky), čistý neprevádzkový | 16.49 | 13.436 | 7.732 | -5.064 | -6.754 |
Iné, Net | -15.285 | 0.649 | 4.713 | -12.297 | 0.187 |
Čistý príjem pred zdanením | -112.943 | -44.33 | -46.709 | -102.875 | -64.071 |
Čistý príjem po zdanení | -124.323 | -52.43 | -46.992 | -105.135 | -65.165 |
Menšinový záujem | 0 | ||||
Čistý príjem pred extra. Položky | -124.323 | -52.43 | -46.992 | -105.135 | -65.165 |
Čistý príjem | -124.323 | -52.43 | -46.992 | -105.135 | -65.165 |
Príjem k dispozícii bežnému Extra. Položky | -124.323 | -52.43 | -46.992 | -105.135 | -65.165 |
Príjem k dispozícii bežnému vr. Extra. Položky | -124.323 | -52.43 | -46.992 | -105.135 | -65.165 |
Zriedený čistý príjem | -124.323 | -52.43 | -46.992 | -105.135 | -65.165 |
Zriedený vážený priemer akcií | 142.735 | 142.046 | 141.95 | 141.794 | 141.599 |
Zriedený EPS s výnimkou mimoriadnych položiek | -0.87101 | -0.36911 | -0.33105 | -0.74146 | -0.46021 |
Dividends per Share - Common Stock Primary Issue | 0 | 0 | 0 | 0 | |
Zriedený normalizovaný EPS | -0.87101 | -1.05369 | -0.33105 | -0.74146 | -0.46021 |
Nezvyčajné výdavky (príjem) | |||||
Gain (Loss) on Sale of Assets | 149.604 |
- Výročný
- Štvrťročne
2022 | 2021 | 2020 | 2019 | 2018 | |
---|---|---|---|---|---|
Celkové aktíva | 2202.69 | 2345.05 | 2130.71 | 2720.6 | 2207.89 |
Hotovosť a krátkodobé investície | 1986.87 | 2114.97 | 1892.38 | 2499.54 | 2084.07 |
Hotovosť a ekvivalenty | 276.472 | 869.191 | 397.664 | 683.287 | 278.82 |
Krátkodobé investície | 1710.4 | 1245.78 | 1494.71 | 1816.26 | 1805.25 |
Pohľadávky celkom, netto | 25.538 | 61.896 | 76.204 | 63.034 | 12.759 |
Accounts Receivable - Trade, Net | 25.538 | 61.896 | 76.204 | 63.034 | 12.759 |
Total Inventory | 22.033 | 24.806 | 21.965 | 18.18 | 8.582 |
Other Current Assets, Total | 168.254 | 143.374 | 140.163 | 139.839 | 102.473 |
Total Assets | 2533.88 | 2611.69 | 2389.75 | 3233.11 | 2667.78 |
Property/Plant/Equipment, Total - Net | 255.838 | 196.069 | 181.077 | 166.251 | 132.16 |
Property/Plant/Equipment, Total - Gross | 343.554 | 298.722 | 240.264 | 193.634 | |
Accumulated Depreciation, Total | -87.716 | -102.653 | -74.013 | -61.474 | |
Intangibles, Net | 29.005 | 27.937 | 25.674 | 24.032 | |
Other Long Term Assets, Total | 75.344 | 41.567 | 50.034 | 320.59 | 303.706 |
Total Current Liabilities | 311.561 | 240.55 | 598.898 | 273.005 | 280.294 |
Accounts Payable | 17.921 | 11.904 | 17.199 | 16.067 | 28.66 |
Accrued Expenses | 196.494 | 129.97 | 155.889 | 106.152 | 77.629 |
Notes Payable/Short Term Debt | 0 | 0 | 0 | 0 | 0 |
Current Port. of LT Debt/Capital Leases | 0.32 | 0.926 | 316.11 | 13.749 | |
Other Current Liabilities, Total | 96.826 | 97.75 | 109.7 | 150.786 | 160.256 |
Total Liabilities | 1960.99 | 1839.95 | 1646.47 | 1762.02 | 1619.7 |
Total Long Term Debt | 1182.72 | 1228.02 | 623.529 | 770.3 | 632.971 |
Long Term Debt | 1182.72 | 1228.02 | 623.529 | 770.3 | 632.971 |
Capital Lease Obligations | |||||
Other Liabilities, Total | 466.709 | 371.379 | 424.046 | 505.26 | 567.359 |
Total Equity | 572.887 | 771.737 | 743.282 | 1471.09 | 1048.08 |
Common Stock | 0.142 | 0.141 | 0.14 | 0.14 | 0.138 |
Additional Paid-In Capital | 2059.85 | 1964.17 | 1895.52 | 2203.78 | 2047.25 |
Retained Earnings (Accumulated Deficit) | -1429.62 | -1159.9 | -1131.31 | -707.534 | -967.293 |
Other Equity, Total | -57.48 | -32.668 | -21.071 | -25.29 | -32.016 |
Total Liabilities & Shareholders’ Equity | 2533.88 | 2611.69 | 2389.75 | 3233.11 | 2667.78 |
Total Common Shares Outstanding | 142.058 | 141.21 | 140.366 | 140.34 | 137.929 |
Minority Interest | 213.453 | 139.081 |
Mar 2023 | Dec 2022 | Sep 2022 | Jun 2022 | Mar 2022 | |
---|---|---|---|---|---|
Celkové aktíva | 2542.62 | 2202.69 | 2152.13 | 2191.15 | 2253.12 |
Hotovosť a krátkodobé investície | 2346.78 | 1986.87 | 1981.66 | 2021.83 | 2052.39 |
Hotovosť a ekvivalenty | 309.031 | 276.472 | 314.993 | 521.917 | 542.513 |
Krátkodobé investície | 2037.75 | 1710.4 | 1666.67 | 1499.91 | 1509.88 |
Pohľadávky celkom, netto | 13.914 | 25.538 | 6.645 | 6.751 | 26.122 |
Accounts Receivable - Trade, Net | 13.914 | 25.538 | 6.645 | 6.751 | 26.122 |
Total Inventory | 22.2 | 22.033 | 20.645 | 19.811 | 24.032 |
Other Current Assets, Total | 159.724 | 168.254 | 143.173 | 142.759 | 150.577 |
Total Assets | 2885.22 | 2533.88 | 2421.97 | 2456.13 | 2519.09 |
Property/Plant/Equipment, Total - Net | 264.306 | 255.838 | 180.806 | 177.015 | 177.724 |
Intangibles, Net | 29.605 | 29.054 | 29.295 | ||
Other Long Term Assets, Total | 78.296 | 75.344 | 59.434 | 58.916 | 58.949 |
Total Current Liabilities | 259.221 | 311.561 | 283.454 | 267.811 | 228.45 |
Accounts Payable | 10.499 | 17.921 | 20.545 | 10.351 | 16.125 |
Accrued Expenses | 130.862 | 189.279 | 158.412 | 159.321 | 115.781 |
Notes Payable/Short Term Debt | 0 | 0 | 0 | 0 | 0 |
Current Port. of LT Debt/Capital Leases | 8.239 | 7.535 | 4.97 | 4.732 | 4.206 |
Other Current Liabilities, Total | 109.621 | 96.826 | 99.527 | 93.407 | 92.338 |
Total Liabilities | 2398.65 | 1960.99 | 1827.61 | 1831.41 | 1809.52 |
Total Long Term Debt | 1184.38 | 1182.72 | 1249.5 | 1248.4 | 1247.93 |
Long Term Debt | 1184.38 | 1182.72 | 1249.5 | 1248.4 | 1247.93 |
Other Liabilities, Total | 955.054 | 466.709 | 294.656 | 315.196 | 333.138 |
Total Equity | 486.57 | 572.887 | 594.361 | 624.726 | 709.574 |
Common Stock | 0.143 | 0.142 | 0.142 | 0.142 | 0.142 |
Additional Paid-In Capital | 2089.36 | 2059.85 | 2034.55 | 2008.79 | 1983.08 |
Retained Earnings (Accumulated Deficit) | -1553.95 | -1429.62 | -1377.19 | -1330.2 | -1225.07 |
Other Equity, Total | -48.983 | -57.48 | -63.14 | -54.007 | -48.578 |
Total Liabilities & Shareholders’ Equity | 2885.22 | 2533.88 | 2421.97 | 2456.13 | 2519.09 |
Total Common Shares Outstanding | 143.023 | 142.058 | 142.017 | 141.831 | 141.753 |
- Výročný
- Štvrťročne
2022 | 2021 | 2020 | 2019 | 2018 | |
---|---|---|---|---|---|
Čistý príjem/Počiatočná čiara | -269.722 | -28.597 | -479.743 | 287.259 | 214.985 |
Hotovosť z prevádzkovej činnosti | -274.37 | 30.799 | 35.892 | 345.627 | 602.906 |
Hotovosť z prevádzkovej činnosti | 14.328 | 15.487 | 13.365 | 12.54 | 10.706 |
Amortization | 2.415 | 2.352 | 2.064 | 1.912 | 1.822 |
Deferred Taxes | 0 | 0 | 341.729 | 0.911 | -290.516 |
Bezhotovostné položky | -28.962 | 155.375 | 232.032 | 211.806 | 166.484 |
Úroky zaplatené v hotovosti | 2.898 | 4.778 | 6.247 | 9.87 | 9.592 |
Zmeny pracovného kapitálu | 7.571 | -113.818 | -73.555 | -168.801 | 499.425 |
Peniaze z investičných činností | -262.636 | 194.906 | 274.477 | -41.274 | -929.563 |
Kapitálové výdavky | -15.721 | -11.955 | -35.12 | -30.905 | -13.608 |
Ostatné investičné položky peňažných tokov, celkom | -246.915 | 206.861 | 309.597 | -10.369 | -915.955 |
Hotovosť z finančných činností | -55.295 | 245.933 | -596.609 | 100.021 | 475.865 |
Financovanie položiek peňažných tokov | -10.982 | -168.954 | -558.097 | -138.354 | 0 |
Vydanie (vyradenie) zásob, netto | 6.373 | 101.317 | -38.512 | 141.375 | 475.865 |
Vydanie (vyradenie) dlhu, netto | -50.686 | 313.57 | 0 | 97 | 0 |
Čistá zmena v hotovosti | -592.719 | 471.527 | -285.623 | 404.467 | 149.19 |
Cash Taxes Paid | 5.01 | 0.038 | 25.855 | 9.041 | 0 |
Devízové efekty | -0.418 | -0.111 | 0.617 | 0.093 | -0.018 |
Mar 2023 | Dec 2022 | Sep 2022 | Jun 2022 | Mar 2022 | |
---|---|---|---|---|---|
Net income/Starting Line | -124.323 | -269.722 | -217.292 | -170.3 | -65.165 |
Cash From Operating Activities | -133.992 | -274.37 | -74.175 | -49.746 | -31.65 |
Cash From Operating Activities | 2.604 | 14.328 | 11.301 | 7.484 | 3.701 |
Amortization | 0.607 | 2.415 | 1.805 | 1.197 | 0.592 |
Deferred Taxes | 0 | ||||
Non-Cash Items | 42.124 | -28.962 | 91.563 | 64.125 | 32.983 |
Cash Taxes Paid | 0.293 | 5.01 | 0.002 | 0.002 | 0.002 |
Cash Interest Paid | 0.089 | 2.898 | 2.204 | 1.544 | 0.594 |
Changes in Working Capital | -55.004 | 7.571 | 38.448 | 47.748 | -3.761 |
Cash From Investing Activities | -325.64 | -262.636 | -474.783 | -290.853 | -287.549 |
Capital Expenditures | -10.472 | -15.721 | -11.582 | -6.04 | -2.705 |
Other Investing Cash Flow Items, Total | -315.168 | -246.915 | -463.201 | -284.813 | -284.844 |
Cash From Financing Activities | 492.087 | -55.295 | -4.276 | -6.11 | -7.325 |
Financing Cash Flow Items | 489.566 | -10.982 | -10.217 | -9.572 | -9.173 |
Issuance (Retirement) of Stock, Net | 2.56 | 6.373 | 6.03 | 3.462 | 1.848 |
Foreign Exchange Effects | 0.104 | -0.418 | -0.964 | -0.565 | -0.154 |
Net Change in Cash | 32.559 | -592.719 | -554.198 | -347.274 | -326.678 |
Issuance (Retirement) of Debt, Net | -0.039 | -50.686 | -0.089 | 0 |
Meno investora | Typ investora | Percento vynikajúce | Držané akcie | Zmena akcií | Dátum držby | Hodnotenie obratu |
---|---|---|---|---|---|---|
Fidelity Management & Research Company LLC | Investment Advisor | 14.9808 | 21436334 | 128815 | 2023-03-31 | LOW |
The Vanguard Group, Inc. | Investment Advisor/Hedge Fund | 9.7482 | 13948885 | 429096 | 2023-03-31 | LOW |
T. Rowe Price Investment Management, Inc. | Investment Advisor | 9.1298 | 13064047 | 1385788 | 2023-03-31 | MED |
Bellevue Asset Management AG | Investment Advisor | 6.6474 | 9511900 | -232000 | 2023-03-31 | LOW |
BlackRock Institutional Trust Company, N.A. | Investment Advisor | 4.9323 | 7057705 | -70015 | 2023-03-31 | LOW |
ClearBridge Investments, LLC | Investment Advisor/Hedge Fund | 3.7679 | 5391581 | -34061 | 2023-03-31 | LOW |
State Street Global Advisors (US) | Investment Advisor/Hedge Fund | 2.8432 | 4068334 | -150395 | 2023-03-31 | LOW |
T. Rowe Price Associates, Inc. | Investment Advisor | 2.6508 | 3793044 | -359563 | 2023-03-31 | LOW |
Tweedy, Browne Company LLC | Investment Advisor | 2.4747 | 3541046 | -90 | 2023-03-31 | LOW |
Deep Track Capital LP | Hedge Fund | 1.9806 | 2834069 | 1628296 | 2023-03-31 | HIGH |
ARK Investment Management LLC | Investment Advisor | 1.843 | 2637192 | -36346 | 2023-03-31 | LOW |
BVF Partners L.P. | Hedge Fund | 1.7896 | 2560761 | 1438952 | 2023-03-31 | LOW |
OrbiMed Advisors, LLC | Investment Advisor/Hedge Fund | 1.4847 | 2124500 | 130900 | 2023-03-31 | LOW |
Geode Capital Management, L.L.C. | Investment Advisor/Hedge Fund | 1.4466 | 2069950 | 57227 | 2023-03-31 | LOW |
Camber Capital Management LP | Hedge Fund | 1.3453 | 1925000 | 0 | 2023-03-31 | MED |
First Trust Advisors L.P. | Investment Advisor | 1.1454 | 1638943 | -141990 | 2023-03-31 | LOW |
Macquarie Investment Management | Investment Advisor | 1.044 | 1493903 | 2216 | 2023-03-31 | LOW |
Norges Bank Investment Management (NBIM) | Sovereign Wealth Fund | 0.9062 | 1296647 | 511086 | 2022-12-31 | LOW |
Charles Schwab Investment Management, Inc. | Investment Advisor | 0.8291 | 1186393 | -69875 | 2023-03-31 | LOW |
Pictet Asset Management Ltd. | Investment Advisor/Hedge Fund | 0.7778 | 1113042 | 739456 | 2023-03-31 | LOW |
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Ionis Pharmaceuticals Company profile
O spoločnosti Ionis Pharmaceuticals, Inc.
Spoločnosť Ionis Pharmaceuticals, Inc. sa zaoberá objavovaním a vývojom liečiv zameraných na ribonukleové kyseliny (RNA). Spoločnosť sa zameriava predovšetkým na svoje kardiovaskulárne a neurologické franšízy. Medzi jej produkty patria SPINRAZA, TEGSEDI a WAYLIVRA. SPINRAZA je určená na liečbu pacientov všetkých vekových kategórií so spinálnou svalovou atrofiou (SMA), progresívnym, vyčerpávajúcim a často smrteľným genetickým ochorením. TEGSEDI je určený na liečbu pacientov s polyneuropatiou spôsobenou dedičnou transtyretinovou (TTR) amyloidózou (hATTR), vysilujúcim, progresívnym a fatálnym ochorením. WAYLIVRA je antisenzitívny liek indikovaný ako doplnok k diéte u dospelých pacientov. Spoločnosť má viac ako šesť liekov v štúdiách fázy III pre osem indikácií, medzi ktoré patria Eplontersen (TTR), Olezarsen (ApoC-III), Donidalorsen (PKK), ION363 (FUS), Pelacarsen (Apo(a)) a Tofersen (SOD1). Kardiovaskulárne lieky vo vývoji zahŕňajú Eplontersen, Olezarsen, Pelacarsen, ION449 (PCSK9), Fesomersen a IONIS-AGT-LRx.
Industry: | Biotechnology & Medical Research (NEC) |
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CALIFORNIA 92010
US
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