Medicure completes enrollment in MEND-PNPO Phase 3 trial of MC-1 for PNPO deficiency
- Medicure completed patient enrollment in the MEND-PNPO Phase 3 trial of MC-1 for PNPO deficiency, reaching its target of 10 patients.
- Participants are moving through treatment and follow-up, positioning the program toward a potential future NDA submission.
- Trial design and baseline data were already presented at the European Epilepsy Congress.
- The same data will be presented later this year at the Child Neurology Society Annual Meeting and the American Epilepsy Society Annual Meeting.
- MC-1 holds FDA Rare Pediatric Disease, Orphan Drug, Fast Track designations, supporting a faster review pathway and potential Priority Review Voucher eligibility.
Disclaimer: This news brief was created by Public Technologies (PUBT) using generative artificial intelligence. While PUBT strives to provide accurate and timely information, this AI-generated content is for informational purposes only and should not be interpreted as financial, investment, or legal advice. Medicure Inc. published the original content used to generate this news brief via ACCESS Newswire (Ref. ID: 202609281800ACCESSWRNAPR_____1228105) on September 28, 2026, and is solely responsible for the information contained therein.